Re: Harvard HCM Genetics Treatment Breakthrough!
Interesting research, but I think it's important to realize this won't be a cure for everybody. In this expertiment they block the mutated gene, so less of the protein it encodes for gets produced. That's great if this protein poisons the normal function of the sarcomere. That's not always the case though. In the mutation I have not enough of the right protein gets produced. My guess is that silencing the gene on the other chromsome wouldn't do very much for me.
Some people say I don't have a heart, but my doctor says I have too much?